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Data updated: Mar 10, 2026

EMPAVELI

PEGCETACOPLAN Complement Inhibitors
Immunology Approved 2021-05-14
3
Indications
--
Phase 3 Trials
2
Priority Reviews
4
Years on Market

Details

Status
Prescription
First Approved
2021-05-14
Routes
SUBCUTANEOUS
Dosage Forms
SOLUTION

Companies

Active Ingredient: PEGCETACOPLAN

EMPAVELI Approval History

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What EMPAVELI Treats

3 indications

EMPAVELI is approved for 3 conditions since its original approval in 2021. These indications span multiple therapeutic areas including oncology, immunology, and more.

  • Paroxysmal Nocturnal Hemoglobinuria
  • C3 Glomerulopathy
  • Membranoproliferative Glomerulonephritis
Source: FDA Label

EMPAVELI Boxed Warning

SERIOUS INFECTIONS CAUSED BY ENCAPSULATED BACTERIA EMPAVELI, a complement inhibitor, increases the risk of serious infections, especially those caused by encapsulated bacteria, such as Streptococcus pneumoniae , Neisseria meningitidis , and Haemophilus influenzae type B [see Warnings and Precautions (5.1) ] . Life-threatening and fatal infections with encapsulated bacteria have occurred in patients treated with complement inhibitors. These infections may become rapidly life-threatening or fatal ...

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Active Pipeline

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Ongoing clinical trials by development phase

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Key Completed Trials

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Completed studies with published results, ranked by significance

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Trial Timeline

Full development history with FDA approval milestones

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Understanding FDA Approval Types
Count Type What it means
- ORIG Original approval - drug first enters market
- SUPPL - Efficacy New indication (new disease/condition approved)
- SUPPL - Labeling Label text changes (warnings, dosing updates)
- SUPPL - Manufacturing Production changes (new facility)
- SUPPL - Chemistry Formulation changes (new dosage strength)

Green lines in the timeline show ORIG and Efficacy approvals - the clinically meaningful milestones.

EMPAVELI FDA Label Details

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Indications & Usage

FDA Label (PDF)

EMPAVELI is a complement inhibitor indicated: for the treatment of adult patients with paroxysmal nocturnal hemoglobinuria (PNH). for the treatment of adult and pediatric patients aged 12 years and older with C3 glomerulopathy (C3G) or primary immune-complex membranoproliferative glomerulonephritis (IC-MPGN), to reduce proteinuria. 1.1 Paroxysmal Nocturnal Hemoglobinuria EMPAVELI ® is indicated for the treatment of adult patients with paroxysmal nocturnal hemoglobinuria (PNH). 1.2 C3 glomerulopathy or primary immune-complex membranoproliferative glomerulonephritis EMPAVELI ® is indicated for t...

⚠️ BOXED WARNING

WARNING: SERIOUS INFECTIONS CAUSED BY ENCAPSULATED BACTERIA EMPAVELI, a complement inhibitor, increases the risk of serious infections, especially those caused by encapsulated bacteria, such as Streptococcus pneumoniae , Neisseria meningitidis , and Haemophilus influenzae type B [see Warnings and Pr...

EMPAVELI Patents & Exclusivity

Latest Patent: Dec 2038
Exclusivity: Jul 2028

Patents (27 active)

US12290566 Expires Dec 14, 2038
US11844841 Expires Dec 9, 2038
US11040107 Expires Apr 9, 2038
US11292815 Expires Nov 15, 2033
US10875893 Expires Nov 15, 2033
US10035822 Expires Nov 15, 2033
US10125171 Expires Aug 2, 2033
US11661441 Expires Jan 13, 2033
US7989589 Expires Dec 4, 2027
US7888323 Expires Dec 4, 2027
+ 17 more patents

Exclusivity

I-972 Until Jul 2028
M-288 Until Feb 2026
NCE Until May 2026
ODE-351 Until May 2028
Source: FDA Orange Book

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Data Sources

Data sourced from official FDA and NIH databases. Click links to verify on original sources.